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Case report: Successful treatment of a patient presenting with a very rare association of acute lymphoblastic leukemia and mucopolysaccharidosis type IVA
2025 Arnaboldi, S; Faraguna, M; Colombini, A; Sala, A; Leoni, V; Spinelli, M; Gotti, G; Bettini, L; Crescitelli, V; Commone, A; Gasperini, S; Rizzari, C
Eight-year national multicenter experience on the use of glucarpidase as effective rescue therapy for delayed methotrexate elimination after high-dose methotrexate cycles administered in children with hemato-oncological diseases
2025 Peccatori, N; Coppola, M; Colombini, A; Silvestri, D; Bertorello, N; Kiren, V; Melchionda, F; Mura, R; Onofrillo, D; Gobbi, S; Mattera, R; Vinti, L; Casini, T; Santoro, N; Sperli, D; D'Ippolito, C; Conter, V; Biondi, A; Rizzari, C
Molecularly Targeted Small Molecule Inhibitor Therapy for Pediatric Acute Lymphoblastic Leukemia: A Comprehensive Review of Clinical Trials
2025 Peccatori, N; Brivio, E; Lissat, A; Bautista Sirvent, F; Salzer, E; Biondi, A; Fazio, G; Rizzari, C; Tasian, S; Zwaan, C
First-Line Postremission Blinatumomab as Successful Toxicity-Sparing Strategy in a Boy with Cystic Fibrosis and Acute Lymphoblastic Leukemia
2025 Peccatori, N; Di Majo, B; Claut, L; Colombini, A; Gotti, G; Leoni, V; Lucchini, G; Sala, A; Spinelli, M; Balduzzi, A; Rizzari, C; Bettini, L
Asparagine transport through SLC1A5/ASCT2 and SLC38A5/SNAT5 is essential for BCP‐ALL cell survival and a potential therapeutic target
2024 Taurino, G; Dander, E; Chiu, M; Pozzi, G; Maccari, C; Starace, R; Silvestri, D; Griffini, E; Bianchi, M; Carubbi, C; Andreoli, R; Mirandola, P; Valsecchi, M; Rizzari, C; D'Amico, G; Bussolati, O
Combined CAR-T/HSCT approach in a patient with refractory acute lymphoblastic leukemia and cystic fibrosis
2024 Di Majo, B; Vendemini, F; Bonanomi, S; Casartelli, P; Napolitano, S; Ottaviano, G; Prunotto, G; Verna, M; Sala, A; Migliorino, G; Petrella, F; Rosso, L; Claut, L; Rafaniello Raviele, P; Rizzari, C; Biondi, A; Balduzzi, A; Lucchini, G
Prenatal origin of NUTM1 gene rearrangement in infant B-cell precursor acute lymphoblastic leukaemia
2024 Bardini, M; Fazio, G; Abascal, L; Meyer, C; Maglia, O; Sala, S; Palamini, S; Rebellato, S; Marschalek, R; Rizzari, C; Biondi, A; Cazzaniga, G
Four Additional Doses of PEG-L-Asparaginase during the Consolidation Phase in the AIEOP-BFM ALL 2009 Protocol Do Not Improve Outcome and Increase Toxicity in High-Risk ALL: Results of a Randomized Study
2024 Conter, V; Valsecchi, M; Cario, G; Zimmermann, M; Attarbaschi, A; Stary, J; Niggli, F; Dalla Pozza, L; Elitzur, S; Silvestri, D; Locatelli, F; Moricke, A; Engstler, G; Smisek, P; Bodmer, N; Barbaric, D; Izraeli, S; Rizzari, C; Boos, J; Buldini, B; Zucchetti, M; Von Stackelberg, A; Matteo, C; Lehrnbecher, T; Lanvers-Kaminsky, C; Cazzaniga, G; Gruhn, B; Biondi, A; Schrappe, M
Hypersensitivity Reactions to Native E. coli L-asparaginase in Children with Acute Lymphoblastic Leukemia Treated in Trial ALL-BFM 2000: Impact of Treatment Schedule and Type of Glucocorticoid in Induction
2023 Moricke, A; Rizzari, C; Alten, J; Attarbaschi, A; Beier, R; Biondi, A; Burkhardt, B; Bodmer, N; Boos, J; Cario, G; Conter, V; Flotho, C; Kulozik, A; Lanvers-Kaminsky, C; Mann, G; Niggli, F; Silvestri, D; Von Stackelberg, A; Stanulla, M; Valsecchi, M; Schrappe, M; Zimmermann, M
Improved survival and MRD remission with blinatumomab vs. chemotherapy in children with first high-risk relapse B-ALL
2023 Locatelli, F; Zugmaier, G; Rizzari, C; Morris, J; Gruhn, B; Klingebiel, T; Parasole, R; Linderkamp, C; Flotho, C; Petit, A; Micalizzi, C; Zeng, Y; Desai, R; Kormany, W; Eckert, C; Moricke, A; Sartor, M; Hrusak, O; Peters, C; Saha, V; Vinti, L; von Stackelberg, A
Incidence and Characteristics of Hypersensitivity Reactions to PEG-asparaginase Observed in 6136 Children with Acute Lymphoblastic Leukemia Enrolled in the AIEOP-BFM ALL 2009 Study Protocol
2023 Rizzari, C; Möricke, A; Valsecchi, M; Conter, V; Zimmermann, M; Silvestri, D; Attarbaschi, A; Niggli, F; Barbaric, D; Stary, J; Elitzur, S; Cario, G; Vinti, L; Boos, J; Zucchetti, M; Lanvers-Kaminsky, C; Von Stackelberg, A; Biondi, A; Schrappe, M
Pharmacological and clinical monitoring in children with acute lymphoblastic leukemia treated with a biogeneric PEG-l-asparaginase product
2022 Matteo, C; Colombini, A; Bettini, L; Porcu, L; Barzaghi, S; Ceruti, T; Silvestri, D; Amoroso, A; Dell'Acqua, F; Gotti, G; Nastasi, C; Zucchetti, M; Rizzari, C
NUP214–ABL1 fusion in childhood T-ALL
2022 Veltri, G; Sandei, M; Silvestri, D; Bresolin, S; Pession, A; Santoro, N; Ziino, O; Veltroni, M; Rizzari, C; Biffi, A; Valsecchi, M; Conter, V; Buldini, B; Accordi, B; Serafin, V
Osteonecrosis in paediatric acute lymphoblastic leukaemia: Incidence, risk factors, radiological patterns and evolution in a single-centre cohort
2022 Brivio, E; Cossio, A; Borra, D; Silvestri, D; Prunotto, G; Colombini, A; Verna, M; Rizzari, C; Biondi, A; Conter, V; Valsecchi, M; Balduzzi, A
Pre-existing antibodies against polyethylene glycol reduce asparaginase activities on first administration of pegylated E. coli asparaginase in children with acute lymphocytic leukemia
2022 Khalil, A; Wurthwein, G; Golitsch, J; Hempel, G; Fobker, M; Gerss, J; Moricke, A; Zimmermann, M; Smisek, P; Zucchetti, M; Nath, C; Attarbaschi, A; Von Stackelberg, A; Gokbuget, N; Rizzari, C; Conter, V; Schrappe, M; Boos, J; Lanvers-Kaminsky, C
Prognostic significance of chromosomal abnormalities at relapse in children with relapsed acute myeloid leukemia: A retrospective cohort study of the Relapsed AML 2001/01 Study
2022 Klein, K; Beverloo, H; Zimmermann, M; Raimondi, S; von Neuhoff, C; de Haas, V; van Weelderen, R; Cloos, J; Abrahamsson, J; Bertrand, Y; Dworzak, M; Fynn, A; Gibson, B; Ha, S; Harrison, C; Hasle, H; Elitzur, S; Leverger, G; Maschan, A; Razzouk, B; Reinhardt, D; Rizzari, C; Smisek, P; Creutzig, U; Kaspers, G
Mucopolysaccharidosis-Plus Syndrome, a Rapidly Progressive Disease: Favorable Impact of a Very Prolonged Steroid Treatment on the Clinical Course in a Child
2022 Faraguna, M; Musto, F; Crescitelli, V; Iascone, M; Spaccini, L; Tonduti, D; Fedeli, T; Kullmann, G; Canonico, F; Cattoni, A; Dell'Acqua, F; Rizzari, C; Gasperini, S
FLT3-ITD in Children with Early T-cell Precursor (ETP) Acute Lymphoblastic Leukemia: Incidence and Potential Target for Monitoring Minimal Residual Disease (MRD)
2022 Locatelli, F; Lo Nigro, L; Andriano, N; Buldini, B; Silvestri, D; Villa, T; Parasole, R; Barisone, E; Testi, A; Biondi, A; Valsecchi, M; Rizzari, C; Conter, V; Basso, G; Cazzaniga, G
PAX5 fusion genes are frequent in poor risk childhood acute lymphoblastic leukaemia and can be targeted with BIBF1120
2022 Fazio, G; Bresolin, S; Silvestri, D; Quadri, M; Saitta, C; Vendramini, E; Buldini, B; Palmi, C; Bardini, M; Grioni, A; Rigamonti, S; Galbiati, M; Mecca, S; Savino, A; Peloso, A; Tu, J; Bhatia, S; Borkhardt, A; Micalizzi, C; Lo Nigro, L; Locatelli, F; Conter, V; Rizzari, C; Valsecchi, M; Te Kronnie, G; Biondi, A; Cazzaniga, G
Challenging Management of Severe Differentiation Syndrome in Pediatric Acute Promyelocytic Leukemia Treated with ATRA/ATO
2022 Molinaro, A; Zanta, D; Moleti, M; Giona, F; Conter, V; Rizzari, C; Biondi, A; Testi, A
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