Sfoglia per Autore
PAX5 fusion genes are frequent in poor risk childhood acute lymphoblastic leukaemia and can be targeted with BIBF1120
2022 Fazio, G; Bresolin, S; Silvestri, D; Quadri, M; Saitta, C; Vendramini, E; Buldini, B; Palmi, C; Bardini, M; Grioni, A; Rigamonti, S; Galbiati, M; Mecca, S; Savino, A; Peloso, A; Tu, J; Bhatia, S; Borkhardt, A; Micalizzi, C; Lo Nigro, L; Locatelli, F; Conter, V; Rizzari, C; Valsecchi, M; Te Kronnie, G; Biondi, A; Cazzaniga, G
Global effort to evacuate Ukrainian children with cancer and blood disorders who have been affected by war
2022 Agulnik, A; Kizyma, R; Salek, M; Wlodarski, M; Pogorelyy, M; Oszer, A; Yakimkova, T; Nogovitsyna, Y; Dutkiewicz, M; Dalle, J; Dirksen, U; Eggert, A; Fernandez-Teijeiro, A; Greiner, J; Kraal, K; Mueller, A; Sramkova, L; Zecca, M; Wise, P; Mlynarski, W; Avula, M; Adyrov, M; Berlanga, P; Blackwood, C; Bouffet, E; Czauderna, P; de Koning, L; dos Reis Farinha, N; Foster, W; Graetz, D; Gupta, S; Holter, W; Hough, R; Kliuchkivska, K; Kolenova, A; Kolodrubiec, J; Moreira, D; Mukkada, S; Mykychak, I; Raciborska, A; Salman, Z; Sopilnyak, A; Tyupa, S; Vinitsky, A; Wobst, N; Miller, B; Rasul, S; Rodriguez-Galindo, C; Alanbousi, I; Alexander, S; Apel, A; Bal, W; Balwierz, W; Basset-Salom, L; Bastardo Blanco, D; Bauer, K; Bayazitov, I; Bhakta, N; Bien, E; Bieniek, K; Blair, S; Bodak, K; Bordeianu, I; Braganca, J; Bucurenci, M; Budny, E; Budzyn, A; Bumgardner, C; Burditt, R; Burnside Clapp, V; Bykov, V; Canete, A; Carnelli, M; Cela, E; Cepowska, Z; Chaber, R; Cherner-Drieux, A; Chubata, M; Clough, H; Czernicka - Siwecka, J; Czyzewski, K; Dashchakovska, O; Dembowska-Baginska, B; Derwich, K; Dommett, R; Dorosh, O; Drabko, K; Dragomir, M; Dworzak, M; Dyma, S; Earl, J; English, M; Evseev, D; Farren, B; Fedyk, N; Ferneza, S; Fox Irwin, L; Galazkowski, R; Ganieva, G; Garanzha, V; Gelman, M; Godzinski, J; Goeres, A; Golban, R; Griksaitis, M; Hampel, M; Hastings, S; Heenen, D; Hill, M; Holiuk, I; Hutnik, L; Irga-Jaworska, N; Istomin, O; Janczar, S; Kacharian, A; Kalwak, K; Karolczyk, G; Karpenko, N; Katsubo, H; Kaznowska, B; Kentsis, A; Ketteler, P; Kienesberger, A; Kiselev, R; Kizyma, Z; Klymniuk, H; Kostiuk, Y; Kowalik, T; Kozlova, O; Kozubenko, V; Kramar, T; Krawczuk-Rybak, M; Kulemzina, I; Kurkowska, P; Kuzyk, A; Ladenstein, R; Laguna, P; Lassaletta, A; Lehmberg, K; Leontieva, O; Liashenko, S; Loizou, L; Lucchetta, S; Lupo, M; Lysytsia, L; Lysytsia, O; Machnik, K; Mainland, J; Matczak, K; Matysiak, M; Mayeur, P; Minervina, A; Mishkova, V; Mizia-Malarz, A; Morales La Madrid, A; Moreno, L; Moskvin, V; Muszynska-Roslan, K; Nelson, A; Ociepa, T; Oltolini, S; Onipko, N; Pappas, A; Patel, A; Patrahau, A; Pauley, J; Pavlenko, Y; Pavlovych, A; Peregud-Pogorzelski, J; Perek-Polnik, M; Perez, V; Perez-Martinez, A; Pikman, Y; Pitozzi, G; Portugal, R; Posternak, V; Prete, A; Pritchard-Jones, K; Radaelli, A; Reeves, T; Reinhardt, D; Reshetnyak, A; Rider, A; Rizzari, C; Rizzi, D; Rodriguez Hermosillo, K; Ronenko, O; Rostowska, A; Rudko, L; Sakaan, F; Sakhar, N; Savva, N; Scaccaglia, D; Schaeffer, E; Schneider, C; Scobie, N; Semeniuk, O; Shevchyk, R; Shuler, A; Shvets, S; Skoczen, S; Smeal, W; Sokolowski, I; Sonkin, A; Stepanjuk, A; Spota, A; Sterba, J; Styczynski, J; Svintsova, O; Synyuta, A; Szczepanski, T; Szczucinski, P; Szmyd, B; Tasso Cereceda, M; Teliuk, A; Tomanek, I; Topping, P; Torrent, M; Trelinska, J; Troyanovska, O; Trubnikova, E; Tsurkan, L; Tsymbalyuk-Voloshyn, I; Urasinski, T; Urbanek-Dadela, A; Vasilieva, N; Vasilyeva, A; Verdu-Amoros, J; Vilcu-Bajurean, N; Vinitsky, L; Volpe, G; Vorobel, O; Wachowiak, J; Wasiak, M; Wiedower, L; Wuenschel, L; Wysocki, M; Yurieva, M; Zagurska, A; Zakharenko, S; Zakharenko, A; Zapotochna, K; Zawitkowska, J
FLT3-ITD in Children with Early T-cell Precursor (ETP) Acute Lymphoblastic Leukemia: Incidence and Potential Target for Monitoring Minimal Residual Disease (MRD)
2022 Locatelli, F; Lo Nigro, L; Andriano, N; Buldini, B; Silvestri, D; Villa, T; Parasole, R; Barisone, E; Testi, A; Biondi, A; Valsecchi, M; Rizzari, C; Conter, V; Basso, G; Cazzaniga, G
The impact of the EU General Data Protection Regulation on childhood cancer research in Europe
2022 Vassal, G; Lazarov, D; Rizzari, C; Szczepanski, T; Ladenstein, R; Kearns, P
Challenging Management of Severe Differentiation Syndrome in Pediatric Acute Promyelocytic Leukemia Treated with ATRA/ATO
2022 Molinaro, A; Zanta, D; Moleti, M; Giona, F; Conter, V; Rizzari, C; Biondi, A; Testi, A
Pre-existing antibodies against polyethylene glycol reduce asparaginase activities on first administration of pegylated E. coli asparaginase in children with acute lymphocytic leukemia
2022 Khalil, A; Wurthwein, G; Golitsch, J; Hempel, G; Fobker, M; Gerss, J; Moricke, A; Zimmermann, M; Smisek, P; Zucchetti, M; Nath, C; Attarbaschi, A; Von Stackelberg, A; Gokbuget, N; Rizzari, C; Conter, V; Schrappe, M; Boos, J; Lanvers-Kaminsky, C
Prognostic significance of chromosomal abnormalities at relapse in children with relapsed acute myeloid leukemia: A retrospective cohort study of the Relapsed AML 2001/01 Study
2022 Klein, K; Beverloo, H; Zimmermann, M; Raimondi, S; von Neuhoff, C; de Haas, V; van Weelderen, R; Cloos, J; Abrahamsson, J; Bertrand, Y; Dworzak, M; Fynn, A; Gibson, B; Ha, S; Harrison, C; Hasle, H; Elitzur, S; Leverger, G; Maschan, A; Razzouk, B; Reinhardt, D; Rizzari, C; Smisek, P; Creutzig, U; Kaspers, G
Mucopolysaccharidosis-Plus Syndrome, a Rapidly Progressive Disease: Favorable Impact of a Very Prolonged Steroid Treatment on the Clinical Course in a Child
2022 Faraguna, M; Musto, F; Crescitelli, V; Iascone, M; Spaccini, L; Tonduti, D; Fedeli, T; Kullmann, G; Canonico, F; Cattoni, A; Dell'Acqua, F; Rizzari, C; Gasperini, S
Impact of Antibodies Against Polyethylene Glycol on the Pharmacokinetics of PEGylated Asparaginase in Children with Acute Lymphoblastic Leukaemia: A Population Pharmacokinetic Approach
2022 Siebel, C; Lanvers-Kaminsky, C; Alten, J; Smisek, P; Nath, C; Rizzari, C; Boos, J; Wurthwein, G
Inotuzumab ozogamicin as single agent in pediatric patients with relapsed and refractory acute lymphoblastic leukemia: results from a phase II trial
2022 Pennesi, E; Michels, N; Brivio, E; van der Velden, V; Jiang, Y; Thano, A; Ammerlaan, A; Boer, J; Beverloo, H; Sleight, B; Chen, Y; Vormoor-Burger, B; Rives, S; Bielorai, B; Rossig, C; Petit, A; Rizzari, C; Engstler, G; Stary, J; Bautista Sirvent, F; Chen-Santel, C; Bruno, B; Bertrand, Y; Rialland, F; Plat, G; Reinhardt, D; Vinti, L; Von Stackelberg, A; Locatelli, F; Zwaan, C
Blinatumomab in Children and Adolescents with Relapsed/Refractory B Cell Precursor Acute Lymphoblastic Leukemia: A Real-Life Multicenter Retrospective Study in Seven AIEOP (Associazione Italiana di Ematologia e Oncologia Pediatrica) Centers
2022 Beneduce, G; De Matteo, A; Stellato, P; Testi, A; Bertorello, N; Colombini, A; Putti, M; Rizzari, C; Cesaro, S; Cellini, M; Barisone, E; Petruzziello, F; Menna, G; Parasole, R
Daratumumab with or without chemotherapy in relapsed and refractory acute lymphoblastic leukemia. A retrospective observational Campus ALL study
2022 Cerrano, M; Bonifacio, M; Olivi, M; Curti, A; Malagola, M; Dargenio, M; Scattolin, A; Papayannidis, C; Forghieri, F; Gurrieri, C; Tanasi, I; Zappasodi, P; Starza, R; Fracchiolla, N; Chiusolo, P; Giaccone, L; Del Principe, M; Giglio, F; Defina, M; Favre, C; Rizzari, C; Castella, B; Pizzolo, G; Ferrara, F; Chiaretti, S; Foa, R
Biological therapies in monogenic autoinflammatory diseases: Long-term efficacy and safety
2021 Pelagatti, M; Cattoni, A; Rizzari, C
A novel homozygous disruptive PRF1 variant (K285Sfs*4) causes very early-onset of familial hemophagocytic lymphohystiocytosis type 2
2021 Saettini, F; Castelli, I; Provenzi, M; Fazio, G; Quadri, M; Cazzaniga, G; Sala, S; Dell'Acqua, F; Sieni, E; Coniglio, M; Pezzoli, L; Iascone, M; Vendemini, F; Balduzzi, A; Biondi, A; Rizzari, C; Bonanomi, S
ALL blasts drive primary mesenchymal stromal cells to increase asparagine availability during asparaginase treatment
2021 Chiu, M; Taurino, G; Dander, E; Bardelli, D; Fallati, A; Andreoli, R; Bianchi, M; Carubbi, C; Pozzi, G; Galuppo, L; Mirandola, P; Rizzari, C; Tardito, S; Biondi, A; D'Amico, G; Bussolati, O
Musculoskeletal manifestations of childhood cancer and differential diagnosis with juvenile idiopathic arthritis (ONCOREUM): a multicentre, cross-sectional study
2021 Civino, A; Alighieri, G; Prete, E; Caroleo, A; Magni-Manzoni, S; Vinti, L; Romano, M; Santoro, N; Filocamo, G; Belotti, T; Santarelli, F; Gorio, C; Ricci, F; Colombini, A; Pastore, S; Cesaro, S; Barone, P; Verzegnassi, F; Olivieri, A; Ficara, M; Miniaci, A; Russo, G; Gallizzi, R; Pericoli, R; Breda, L; Mura, R; Podda, R; Onofrillo, D; Lattanzi, B; Tirtei, E; Maggio, M; De Santis, R; Consolini, R; Arlotta, A; La Torre, F; Mainardi, C; Pelagatti, M; Coassin, E; Capolsini, I; Burnelli, R; Tornesello, A; Soscia, F; De Fanti, A; Rigante, D; Pizzato, C; De Fusco, C; Abate, M; Roncadori, A; Rossi, E; Stabile, G; Biondi, A; Lepore, L; Conter, V; Rondelli, R; Pession, A; Ravelli, A; Amatruda, M; Atzeni, C; Bertolini, P; Bigucci, B; Caniglia, M; Cappella, M; Cattalini, M; Cefalo, M; Cellini, M; Cortis, E; Davi, S; De Benedetti, F; Di Cataldo, A; Fabbri, E; Fagioli, F; Fontanili, I; Garaventa, A; Gicchino, M; Ladogana, S; Locatelli, F; Magnolato, A; Marsili, M; Martino, S; Mascarin, M; Messina, C; Micalizzi, C; Porta, F; Rizzari, C
Recurrent genetic fusions redefine MLL germ line acute lymphoblastic leukemia in infants
2021 Fazio, G; Bardini, M; De Lorenzo, P; Grioni, A; Quadri, M; Pedace, L; Corral Abascal, L; Palamini, S; Palmi, C; Buldini, B; Vinti, L; Parasole, R; Barisone, E; Zecca, M; Favre, C; Locatelli, F; Conter, V; Rizzari, C; Valsecchi, M; Biondi, A; Cazzaniga, G
A phase 2 study of nilotinib in pediatric patients with CML: Long-term update on growth retardation and safety
2021 Hijiya, N; Maschan, A; Rizzari, C; Shimada, H; Dufour, C; Goto, H; Kang, H; Guinipero, T; Karakas, Z; Bautista, F; Ducassou, S; Yoo, K; Zwaan, C; Millot, F; Patterson, B; Samis, J; Aimone, P; Allepuz, A; Titorenko, K; Sosothikul, D
Recommendations by the European Network of Paediatric Research at the European Medicines Agency (Enpr-EMA) Working Group on preparedness of clinical trials about paediatric medicines process
2021 Siapkara, A; Fracasso, C; Egger, G; Rizzari, C; Trasorras, C; Athanasiou, D; Turner, M
Effect of Blinatumomab vs Chemotherapy on Event-Free Survival among Children with High-risk First-Relapse B-Cell Acute Lymphoblastic Leukemia: A Randomized Clinical Trial
2021 Locatelli, F; Zugmaier, G; Rizzari, C; Morris, J; Gruhn, B; Klingebiel, T; Parasole, R; Linderkamp, C; Flotho, C; Petit, A; Micalizzi, C; Mergen, N; Mohammad, A; Kormany, W; Eckert, C; Moricke, A; Sartor, M; Hrusak, O; Peters, C; Saha, V; Vinti, L; Von Stackelberg, A
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