ZECCHILLO, ALESSANDRA
ZECCHILLO, ALESSANDRA
DIPARTIMENTO DI MEDICINA E CHIRURGIA (SCHOOL OF MEDICINE AND SURGERY)
A standardized protocol for assessing immunodeficiency in mouse models
2026 Cappelleri, A; Canesi, S; Capo, V; Zecchillo, A; Notarangelo, L; Draghici, E; Bettoni, V; Martini, V; Moretti, P; Villa, A; Paltrinieri, S; Scanziani, E; Recordati, C
Preclinical modeling of WHIM Syndrome to develop an adenine base editing therapeutic approach
2026 Zecchillo, A; Fiumara, M; Porcellini, S; Canarutto, D; Draghici, E; Iannello, V; Riva, N; Pedrazzani, G; Pereira, J; Warnatz, K; Ehl, S; Murphy, P; Mcdermott, D; Naldini, L; Villa, A; Ferrari, S; Carmina Castiello, M
Cxcr4-R334X mouse: a model to investigate the pathogenesis of WHIM Syndrome and assess novel gene correction therapy
2025 Zecchillo, A; Fiumara, M; Porcellini, S; Canarutto, D; Pedrazzani, G; Iannello, V; Cascio Ferro, A; Pereira, J; Naldini, L; Villa, A; Ferrari, S; Carmina Castiello, M
Cxcr4-R334X mouse: a model to study WHIM syndrome pathogenesis and evaluate innovative gene correction treatment
2025 Zecchillo, A; Fiumara, M; Porcellini, S; Canarutto, D; Pedrazzani, G; Iannello, V; Cascio Ferro, A; Pereira, J; Naldini, L; Villa, A; Ferrari, S; Castiello, M
In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking
2025 Milani, M; Fabiano, A; Perez-Rodriguez, M; Hernandez, R; Zecchillo, A; Zonari, E; Ottonello, S; Basso-Ricci, L; Canepari, C; Volpin, M; Iannello, V; Capo, V; Quaranta, P; Seffin, L; Russo, F; Biffi, M; Ormoli, L; Brombin, C; Carlucci, F; Forlino, A; Filibian, M; Montini, E; Scala, S; Villa, A; Bueren, J; Rio, P; Aiuti, A; Cantore, A; Naldini, L
Preclinical modeling of WHIM Syndrome to develop a base editing therapeutic approach
2025 Zecchillo, A; Fiumara, M; Porcellini, S; Canarutto, D; Draghici, E; Iannello, V; Pedrazzani, G; Pereira, J; Warnatz, K; Ehl, S; Mcdermott, D; Naldini, L; Villa, A; Ferrari, S; Carmina Castiello, M
Correction of osteopetrosis in the neonate oc/oc murine model after lentiviral vector gene therapy and non-genotoxic conditioning
2024 Penna, S; Zecchillo, A; Di Verniere, M; Fontana, E; Iannello, V; Palagano, E; Mantero, S; Cappelleri, A; Rizzoli, E; Santi, L; Crisafulli, L; Filibian, M; Forlino, A; Basso-Ricci, L; Scala, S; Scanziani, E; Schinke, T; Ficara, F; Sobacchi, C; Villa, A; Capo, V
In vivo gene transfer as a new therapeutical approach for autosomal recessive osteopetrosis
2024 Zecchillo, A; Milani, M; Iannello, V; Draghici, E; Fabiano, A; Russo, F; Ottonello, S; Forlino, A; Filibian, M; Cantore, A; Capo, V; Villa, A
Pneumocystis murina lesions in lungs of experimentally infected Cd40l-/- mice
2024 Cappelleri, A; Canesi, S; Bertola, L; Capo, V; Zecchillo, A; Albano, L; Villa, A; Scanziani, E; Recordati, C
Testing lipid nanoparticles as delivery tool for genome editing of murine haematopoietic stem and progenitor cells
2024 Zecchillo, A; Fiumara, M; Porcellini, S; Canarutto, D; Pedrazzani, G; Pereira, J; Naldini, L; Villa, A; Ferrari, S; Carmina Castiello, M
Non-genotoxic conditoning and in vivo gene transfer as new therapeutical approaches for autosomal recessive osteopetrosis
2023 Zecchillo, A; Milani, M; Iannello, V; di Verniere, M; Draghici, E; Santi, L; Penna, S; Fabiano, A; Russo, F; Ottonello, S; Cappelleri, A; Scanziani, E; Sobacchi, C; Forlino, A; Filibian, M; Cantore, A; Capo, V; Villa., A
Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations
2023 Castiello, M; Di Verniere, M; Draghici, E; Fontana, E; Penna, S; Sereni, L; Zecchillo, A; Minuta, D; Uva, P; Zahn, M; Gil-Farina, I; Annoni, A; Iaia, S; Ott De Bruin, L; Notarangelo, L; Pike-Overzet, K; Staal, F; Villa, A; Capo, V
Non-Genotoxic conditioning to implement therapy strategy in Autosomal Recessive Osteopetrosis
2022 Zecchillo, A; Di Verniere, M; Draghici, E; Santi, L; Penna, S; Cappelleri, A; Scanziani, E; Sobacchi, C; Capo, V; Villa, A
Ionic Regulation of T-Cell Function and Anti-Tumour Immunity
2021 Ginefra, P; Carrasco Hope, H; Spagna, M; Zecchillo, A; Vannini, N